Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Β-Thalassemias | NEJM
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Gene Therapy For Beta-Thalassemia: Updated Perspectives | TACG
A paradigm shift on beta-thalassaemia treatment: How will we manage this old disease with new therapies? - ScienceDirect
IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Pathophysiology and treatment of patients with... | F1000Research
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Safety and efficacy of thalidomide in patients with transfusion-dependent β- thalassemia: a randomized clinical trial | Signal Transduction and Targeted Therapy
Β-Thalassemias | NEJM
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
An urgent need for improving thalassemia care due to the wide gap in current real-life practice and clinical practice guidelines | Scientific Reports
Tricuspid-valve regurgitant jet velocity as a risk factor for death in β- thalassemia | Haematologica
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
β-Thalassemia | Genetics in Medicine
2021 update on clinical trials in β‐thalassemia - Musallam - 2021 - American Journal of Hematology - Wiley Online Library
